Cerdelga: Uses, Dosage, Demographic, Side Effects, Interactions, and Generic Options Cerdelga (generic name eliglustat) is a medication used in the treatment of Gaucher Disease Type 1, a rare inherited metabolic disorder that affects the body's ability to break down a fatty substance called glucocerebroside. Cerdelga works in the body by inhibiting the activity of an enzyme called glucosylceramide synthase, which is responsible for the production of glucocerebroside. Uses Cerdelga is used to improve the symptoms of Gaucher Disease Type 1 in adult patients. The medication can help reduce the levels of glucocerebroside in the body, thereby alleviating a wide range of symptoms associated with the disease, such as anemia, bone pain, fatigue, liver and spleen enlargement, and easy bleeding or bruising. Dosage The recommended starting dosage for Cerdelga is 100 mg twice daily, preferably with food. The dosage may be increased to 200 mg twice daily based on the patient's response to treatment and tolerability. The medication should be taken at approximately the same time each day to maintain consistent levels of the drug in the body. Demographic Cerdelga is intended for use in adult patients with Gaucher Disease Type 1. The medication is not approved for use in children or adolescents. Side Effects Like all medications, Cerdelga may cause side effects in some patients. Some of the most common side effects associated with Cerdelga include diarrhea, nausea, vomiting, stomach pain, headache, fatigue, and back pain. These side effects are usually mild to moderate and tend to resolve on their own within a few days. In rare cases, Cerdelga may cause more serious side effects, such as severe allergic reactions, pancreatitis, abnormal liver function, and low platelet count. Patients who experience any of these side effects should seek medical attention immediately. Interactions Cerdelga may interact with certain medications, particularly those that affect the activity of enzymes that metabolize eliglustat. Patients should inform their healthcare provider of any prescription or over-the-counter medications, vitamins, or supplements they are taking before starting treatment with Cerdelga. Generic Options Cerdelga is a branded medication manufactured by Sanofi Genzyme. As of 2021, there are no FDA-approved generic versions of Cerdelga available on the market. However, some patients may be able to obtain eliglustat from other countries where the medication is marketed under different brand names. In conclusion, Cerdelga is an effective treatment option for adult patients with Gaucher Disease Type 1. The medication works by inhibiting the production of glucocerebroside in the body, thereby reducing the symptoms associated with the disease. Patients should ensure that they take the medication as directed by their healthcare provider and report any side effects promptly. Finally, patients should talk to their healthcare provider about any other medications that they are taking before starting treatment with Cerdelga.